# RPE65-associated inherited retinal diseases: consensus recommendations for eligibility to gene therapy

> Research article (Orphanet Journal of Rare Diseases, 2021) · cited 41× · AI/ML

**Wikidata**: [openalex:W3164969949](https://www.wikidata.org/wiki/openalex:W3164969949)  
**Source**: https://4ort.xyz/entity/rpe65-associated-inherited-retinal-diseases-consensus-recommendations-for-eligibility-to-gene-therapy
