# Patient Voice in Rare Disease Drug Development and Endpoints

> Research article (Therapeutic Innovation & Regulatory Science, 2016) · cited 22× · AI/ML

**Wikidata**: [openalex:W2547100341](https://www.wikidata.org/wiki/openalex:W2547100341)  
**Source**: https://4ort.xyz/entity/patient-voice-in-rare-disease-drug-development-and-endpoints
