# Hierarchical Bayesian modelling of disease progression to inform clinical trial design in centronuclear myopathy

> Research article (Orphanet Journal of Rare Diseases, 2021) · cited 30× · AI/ML

**Wikidata**: [openalex:W3120427786](https://www.wikidata.org/wiki/openalex:W3120427786)  
**Source**: https://4ort.xyz/entity/hierarchical-bayesian-modelling-of-disease-progression-to-inform-clinical-trial-design-in-centronuclear-myopathy