# Development of a novel observer reported outcome tool as the primary efficacy outcome measure for a rare disease randomized controlled trial

> Research article (Mitochondrion, 2017) · cited 13× · AI/ML

**Wikidata**: [openalex:W2767544998](https://www.wikidata.org/wiki/openalex:W2767544998)  
**Source**: https://4ort.xyz/entity/development-of-a-novel-observer-reported-outcome-tool-as-the-primary-efficacy-outcome-measure-for-a-rare-disease-randomi