# A Pharmacometric Approach to Substitute for a Conventional Dose-Finding Study in Rare Diseases: Example of Phase III Dose Selection for Emicizumab in Hemophilia A

> Research article (Clinical Pharmacokinetics, 2017) · cited 78× · AI/ML

**Wikidata**: [openalex:W2772289727](https://www.wikidata.org/wiki/openalex:W2772289727)  
**Source**: https://4ort.xyz/entity/a-pharmacometric-approach-to-substitute-for-a-conventional-dose-finding-study-in-rare-diseases-example-of-phase-iii-dose
