# A hierarchical Bayesian approach for combining pharmacokinetic/pharmacodynamic modeling and Phase IIa trial design in orphan drugs: Treating adrenoleukodystrophy with Lorenzo’s oil

> Research article (Journal of Biopharmaceutical Statistics, 2016) · cited 14× · AI/ML

**Wikidata**: [openalex:W2516440946](https://www.wikidata.org/wiki/openalex:W2516440946)  
**Source**: https://4ort.xyz/entity/a-hierarchical-bayesian-approach-for-combining-pharmacokinetic-pharmacodynamic-modeling-and-phase-iia-trial-design-in-or